Molecular Therapies
摘要
This chapter describes the development of molecular therapies for X-linked hypohidrotic ectodermal dysplasia (XLHED), the most common ectodermal dysplasia syndrome, and for the cutaneous and ocular manifestations of p63-associated syndromes. Large parts of the text are based on the following previously published journal article by Holm Schneider: “Ectodermal dysplasias: New perspectives on the treatment of so far immedicable genetic disorders”, Front Genet. 13:1000744, doi: 10.3389/fgene.2022.1000744; available under the terms of the Creative Commons Attribution License (CC BY).