<p>Outcomes following international MDT assessment of adult IEI patients for allogeneic HSCT suggest early referral is vital: patients considered too high risk for transplant have poor outcomes with a 3-year overall survival of 31%.</p>

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Timing is everything: outcomes of allogeneic HSCT in adults with inborn errors of immunity

  • Katharine Orf,
  • Hannah Al Yousuf,
  • Thomas A. Fox,
  • Nadhira Samsudeen,
  • Suzanne Elcombe,
  • Mari Campbell,
  • Stephen Jolles,
  • Niall Conlon,
  • Charu Chopra,
  • Jennifer M. Tjon,
  • Eleni Tholouli,
  • Moira Thomas,
  • Lisa Devlin,
  • Claire Stockdale,
  • Aarnoud Huissoon,
  • Tor Henrik Tvedt,
  • Elizabeth McDermott,
  • Neill Storrar,
  • Hannah Hunter,
  • Francesca Ferrua,
  • Harichandana Ghanta,
  • Olaf Neth,
  • Elisa Codero,
  • Anoop Mistry,
  • Adrian Shields,
  • Sarah Goddard,
  • Arjan J. Kwakernaak,
  • Godelieve de Bree,
  • Franziska Taube,
  • Katja Sockel,
  • Julia Körholz,
  • Carmen Herling,
  • Christian Klemann,
  • Vikram Singh,
  • Veronika Dobsinska,
  • Sarah Johnston,
  • Prashantha Vaitla,
  • Samar Ojaimi,
  • Ravishankar Sargur,
  • Shankara Paneesha,
  • Danielle Blunt,
  • Carsten Schade-Larsen,
  • Valérie Massey,
  • Shreyans Gandhi,
  • Mark Kačar,
  • Fredrik Rorsman,
  • Sinisa Savic,
  • Arpad Toth,
  • Helen Leavis,
  • Maria Carrabba,
  • Pavels Gordins,
  • Sujoy Khan,
  • Simon Bulley,
  • Kiran Tawana,
  • Vanessa Daza-Cajigal,
  • John Snowden,
  • David M. Lowe,
  • Sorena Kiani-Alikhan,
  • Ben Uttenthal,
  • Ariharan Anantharachagan,
  • Catharina Schuetz,
  • Smita Y. Patel,
  • Arian Laurence,
  • Siobhan O. Burns,
  • Venetia Bigley,
  • Emma C. Morris

摘要

Outcomes following international MDT assessment of adult IEI patients for allogeneic HSCT suggest early referral is vital: patients considered too high risk for transplant have poor outcomes with a 3-year overall survival of 31%.