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Efficacy of MEK inhibitors in Erdheim-Chester disease: impact of MAPK pathway pathogenic variants

  • Aldo A. Acosta-Medina,
  • Jithma P. Abeykoon,
  • Saurabh Zanwar,
  • Gordon J. Ruan,
  • Karen L. Rech,
  • Aishwarya Ravindran,
  • N. Nora Bennani,
  • Caroline J. Davidge-Pitts,
  • Matthew J. Koster,
  • Jay H. Ryu,
  • Mithun V. Shah,
  • W. Oliver Tobin,
  • Robert Vassallo,
  • Jason R. Young,
  • Ronald S. Go,
  • Gaurav Goyal
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