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Phase Ib study of PRT543, an oral protein arginine methyltransferase 5 (PRMT5) inhibitor, in patients with advanced splicing factor-mutant myeloid malignancies

  • Jan Philipp Bewersdorf,
  • Xiaoli Mi,
  • Bin Lu,
  • Andrew Kuykendall,
  • David Sallman,
  • Manish Patel,
  • Don Stevens,
  • Alexander Philipovskiy,
  • Grerk Sutamtewagul,
  • Lucia Masarova,
  • Gina Keiffer,
  • Amit Verma,
  • Neha Bhagwat,
  • Min Wang,
  • Andrew Moore,
  • Joseph Rager,
  • Diane Heiser,
  • Sunhee Ro,
  • Wan-Jen Hong,
  • Omar Abdel-Wahab,
  • Eytan M. Stein

摘要