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Sustainable efficacy of nusinersen in children with later-onset spinal muscular atrophy: a 3-year observational study

  • Yi-Jie Feng,
  • Yi-Cheng Yu,
  • Jing-Li Zhao,
  • Lu Xu,
  • Cong-Ying Zhao,
  • Yi Hua,
  • Guo-Xia Sheng,
  • Ting-Ting Chen,
  • Yi Zhang,
  • Lin-Lin Wei,
  • Feng Gao,
  • Shan-Shan Mao
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